2026-02-27 00:00:00:03014252310http://paper.people.com.cn/rmrb/pc/content/202602/27/content_30142523.htmlhttp://paper.people.com.cn/rmrb/pad/content/202602/27/content_30142523.html11921 本版责编:李 拯 邹 翔 常 晋
The CuRe trial is now enrolling up to 35 patients in its Phase 1/2a study. Children will be followed through age 6 to evaluate long-term safety and early signs of improved movement, bladder and bowel function.
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